T cell function is impaired in people living with HIV (PWH) due to an increased expression of immune checkpoints, such as programmed death-1 (PD-1) and cytotoxic T-lymphocyte-associated protein 4 (CTLA-4), leading to immune exhaustion. To obtain effective immune control of HIV, strategies to reverse this exhaustion and increase T cell function are required. One promising approach to improve immune function is blocking immune checkpoints via the administration of monoclonal antibodies that prevent binding to their receptor, thereby reversing T cell exhaustion.
As part of a prospective longitudinal clinical trial of PWH on ART with cancer (AIDS Malignancy Consortium-095 Study), participants received anti-PD-1 (nivolumab) every 2 weeks, with some participants additionally receiving anti-CTLA-4 (ipilimumab) every 6 weeks. We sorted HIV-tetramer+ and tetramer- CD8+ T-cells from 7 participants receiving combination treatment, and 2 participants receiving anti-PD-1 alone, both before and following infusions at weeks 0 and 6. We then performed single-cell RNA sequencing.
In total CD8+ T cells, combination immune checkpoint blockade did not alter the frequency of cellular subsets nor the cellular phenotype within these clusters. In tetramer+ CD8+ T-cells, we observed a modest, transient increase in effector memory T cell frequency following initial immune checkpoint blockade. This contrasts with our previous data from participants who received nivolumab alone. Here, the frequency of tetramer+ effector CD8+ T cells decreased concurrently with the emergence of an exhaustion progenitor cluster with an interferon-stimulated gene signature.
In PWH, we observed minimal changes in the phenotype of antigen-specific T cells following combination immune checkpoint blockade with anti-PD-1 and anti-CTLA-4 antibodies, in contrast with our previous data on single PD-1 blockade. Future work will analyse samples from a greater number of participants to enable detailed characterisation of antigen-specific cells following single and combination immune checkpoint blockade.